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Gene Therapy Study for Late Juvenile Metachromatic Leukodystrophy (LJ MLD)

By February 22, 2022February 23rd, 2022Uncategorized
Gene Therapy Study for Late Juvenile MLD

Following the wonderful news that Gene Therapy was approved for use in England by the NHS for pre-symptomatic Late-Infantile and pre-symptomatic and mildly-symptomatic Early Juvenile MLD, we now have more exciting news! A clinical study for sufferers of pre-symptomatic and early-symptomatic sufferers of Late Juvenile MLD is now recruiting.  The study is being conducted at Ospedale San Raffaele – Telethon Institute for Gene Therapy (OSR-TIGET) in Milan, Italy.

Download full details on the gene therapy study.

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