Uncategorized Gene Therapy Study for Late Juvenile Metachromatic Leukodystrophy (LJ MLD) Following the wonderful news that Gene Therapy was approved for use in England by the…MLD adminFebruary 22, 2022
Research NICE final guidance approves life-changing gene therapy for treating Metachromatic Leukodystrophy (MLD) We are delighted to announce that Atidarsagene autotemcel (Libmeldy®) has been recommended as an option…MLD adminFebruary 4, 2022
