Treating early onset MLD

By December 21, 2020 Families, Research
Libmeldy EU approval for treatment of early onset MLD

We are pleased to report Orchard Therapeutics has received EC full (standard) market approval for Libmeldy, an advanced therapy medicine for the treatment of Early-Onset MLD. A decade after the first patient was treated in clinical trials, a one-time treatment with Libmeldy has been shown to preserve motor and cognitive function. Read the full press release